Literature Review

Gene Replacement Improves Survival in Spinal Muscular Atrophy

Neurology Reviews. 2018 January;26(1):32

 

—Erik Greb

Suggested Reading

Mendell JR, Al-Zaidy S, Shell R, et al. Single-dose gene-replacement therapy for spinal muscular atrophy. N Engl J Med. 2017;377(18):1713-1722.

van der Ploeg AT. The dilemma of two innovative therapies for spinal muscular atrophy. N Engl J Med. 2017;377(18):1786-1787.

Pages

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