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Hemophilia Questionnaire Proves Valid Worldwide

Publish date:: April 3, 2019

Key clinical point: The PROBE questionnaire is a valid instrument to evaluate health status in patients with hemophilia in an international context.

Major finding: The questionnaire had low variability when implemented on a multinational, cross‐cultural level. Region contributed 0.26% of the variance in the PROBE score.

Study details: An international study of 862 participants, with and without hemophilia, from various socioeconomic and cultural backgrounds.

Disclosures: The study was funded by Baxalta, Bayer, Bioverativ, CSL Behring, Novo Nordisk, Roche, and Sobi, with additional support from the U.S. National Hemophilia Foundation. Co-author Mark W. Skinner is the principal investigator and no other investigators reported relevant conflicts of interest.

Commentary:

Chai-Adisaksopha C et al. Haemophilia. 2019 Mar 12. doi: 10.1111/hae.13703.

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