Pediatrics
From the Journals
Stable response in sickle cell disease patient treated with gene therapy
A case study reveals clinical remission and ongoing healthy hemoglobin production 15 months after treatment for sickle cell disease.
News
CCSs’ subsequent cancer risk decreased from ’70s to ’90s
Childhood cancer survivors (CCSs) who were diagnosed in the 1990s have a lower risk of subsequent malignancies than CCSs diagnosed in the 1970s,...
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Study reveals patterns of ED use in SCD patients
Photo courtesy of St.
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B-cell energy levels linked to leukemic transformation
Photo from Business Wire A pair of transcription factors protect B cells from malignant transformation by keeping the cells’ glucose and energy...
News
G-CSF could prevent infertility in cancer patients
Granulocyte colony-stimulating factor (G-CSF) could prevent infertility in male cancer patients, according to preclinical research published in...
Conference Coverage
Boys with severe hemophilia have good physical function
Children with severe hemophilia have generally good self-reported health-related quality of life and physical functioning, but one issue in...
Conference Coverage
Study: No link between vaccines, inhibitor development
Pediatric vaccinations given near the time of factor VIII exposure are not linked with inhibitor development in patients with severe hemophilia A...
News
Therapy demonstrates safety, efficacy in kids with hemophilia B
Photo courtesy of Biogen A recombinant factor IX Fc fusion protein (rFIXFc) has produced favorable results in children with severe hemophilia B,...
News
Kids, parents over-report ALL treatment adherence
New research published in Blood suggests young patients with acute lymphoblastic leukemia (ALL)—and their parents—are likely to over-report...
News
Cheap manufacture of generic cancer drugs is feasible, study shows
Photo courtesy of FDA AMSTERDAM—New research suggests some generic cancer drugs could be manufactured for less than 1% of the prices currently...
News
Donor CAR T cells bridge to HSCT in infants with ALL
New research suggests that “universal,” donor-derived, chimeric antigen receptor (CAR) T cells may be a viable treatment option for very young...