Summaries of Must-Read Clinical Literature, Guidelines, and FDA Actions View by Topic View by Date Must Reads In Rare Diseases Rare Diseases for November/December 2020 Childhood Hodgkin survivors have neurocognitive impairment, More must reads Rare Diseases for September/October 2020 ‘Tour de force’ study reveals therapeutic targets in 38% of cancer patients, More must readsRare Diseases for May/June 2020 Video coaching may relieve anxiety and distress for long-distance cancer caregivers, More must readsRare Diseases for March/April 2020 Accelerated fetal growth in boys associated with development of AML, More must readsRare Diseases for January/February 2020 SCC survival remains poor in epidermolysis bullosa, Deferiprone noninferior to deferoxamine for iron overload in SCD, rare anemias, Expedited Review Programs Not Shortening Drug Development, More must readsPages1 2 last »