News from NORD

Patients Are Being Recruited for LPL-Deficiency Study


 

Adult patients with lipoprotein lipase deficiency (LPLD) in the US and Canada may be eligible for a study of alipogene tiparvovec. LPLD is a rare, autosomal recessive disorder of lipid metabolism. Additional information can be found on clinicaltrials.gov under study ID NCT02904772.

Recommended Reading

Midostaurin cut organ damage in systemic mastocytosis
MDedge Hematology and Oncology
Study tracks distant metastatic patterns of Merkel cell carcinoma
MDedge Hematology and Oncology
Study tracks distant metastatic patterns of Merkel cell carcinoma
MDedge Hematology and Oncology
Study identifies important predictors for PC/PGL
MDedge Hematology and Oncology
Hemophilia drugs top Medicaid spending per prescription
MDedge Hematology and Oncology
Children under 6 with factor XIII deficiency had no major bleeds with recombinant product
MDedge Hematology and Oncology
Sickle cell trait raises exertional rhabdomyolysis risk
MDedge Hematology and Oncology
NORD Urges Congress to Pass 21st Century Cures Act
MDedge Hematology and Oncology
Nominate a Colleague for a NORD 2017 Rare Impact Award
MDedge Hematology and Oncology
Myeloablative HSCT bests IV CYC for systemic scleroderma
MDedge Hematology and Oncology