Anemia
News
Drug granted breakthrough status as first-line SAA therapy
The US Food and Drug Administration (FDA) has granted breakthrough therapy designation to eltrombopag (Promacta®) for use in combination with...
News
FDA grants breakthrough therapy designation for severe aplastic anemia drug
Eltrombopag, from Novartis, will get expedited review for first-line treatment of severe aplastic anemia. It is already approved as a second-line...
News
FDA approves hydroxyurea for pediatric patients with sickle cell anemia
This is the first FDA approval for hydroxyurea in pediatric patients with sickle cell anemia.
News
Drug approved for kids with sickle cell anemia
The US Food and Drug Administration (FDA) has approved a hydroxyurea product (Addmedica’s Siklos) for use in pediatric patients with sickle cell...
From the Journals
Rare neurological complication linked to Waldenstrom disease
A 67-year-old man with Waldenstrom disease experienced bilateral facial nerve palsy.
Conference Coverage
Clinic eases pediatric-adult transition in sickle cell disease
CONCORD, N.C. – Transitional programs could help teenage patients continue self-care and avoid risk behaviors.
News
AVP stimulates red blood cell production
Researchers say they have uncovered a new function of arginine vasopressin (AVP). It seems this hormone does more than maintain fluid balance for...
News
FDA grants drug orphan designation for AML, MDS
The US Food and Drug Administration (FDA) has granted orphan drug designation to AMV564, a CD33/CD3 bispecific antibody, for the treatment of...
From the Journals
Vasopressin stimulates red blood cell production
The findings could have implications for the development of new treatments designed to stimulate RBC production after bleeding, chemotherapy, or...
News
FDA grants priority review to NDA for avatrombopag
The US Food and Drug Administration (FDA) has granted priority review to the new drug application (NDA) for avatrombopag. Avatrombopag is a...
News
Thoughts, emotions linked to opioid use in SCD
Results of a small study suggest that negative thoughts and emotions may increase opioid use in patients with sickle cell disease (SCD)....