Anemia
Conference Coverage
Voxelotor benefits adolescents with SCD
STOCKHOLM—An ongoing phase 2 study suggests voxelotor (GBT440) can benefit adolescents with sickle cell disease (SCD). In the HOPE-KIDS 1 study,...
News
Leading researcher in genetics, hematology dies at 84
George Stamatoyannopoulos, MD, who conducted important research into hemoglobinopathies, passed away this month at the age of 84. Dr...
Conference Coverage
Drug is convenient alternative for PNH, doc says
STOCKHOLM—Results of a phase 3 study suggest the long-acting C5 complement inhibitor ravulizumab produces similar results as eculizumab in...
Conference Coverage
Sickle cell disease exacts a heavy vocational toll
WASHINGTON – “This is a dream deferred” for patients and families affected by sickle cell disease.
Conference Coverage
Family engagement can buffer early cognitive hit from SCD
WASHINGTON –
News
Mircera approved for anemia in pediatric patients with CKD
Mircera®, methoxy polyethylene glycol-epoetin beta, was approved by the US Food and Drug Administration (FDA) to treat anemia in pediatric...
News from the FDA/CDC
FDA approves long-acting ESA for dialysis-related anemia in children, adolescents
Mircera is now indicated for dialysis-related anemia in patients aged 5-17 years with chronic kidney disease.
News
FDA approves first biosimilar pegfilgrastim
The US Food and Drug Association (FDA) has approved pegfilgrastim-jmdb (Fulphila™) as the first biosimilar to Neulasta®. The agents reduce the...
News
Eltrombopag receives priority review designation for SAA
Eltrombopag (Promacta®) in combination with standard immunosuppressive therapy (IST) has received priority review designation from the US Food and...
News
FDA grants priority review to first-line SAA treatment
Eltrombopag is being evaluated for first-line treatment of severe aplastic anemia with standard immunosuppressive therapy.
News
FDA places CTX001 for SCD on clinical hold
The US Food and Drug Administration (FDA) has placed a clinical hold on the investigational new drug application (IND) for CTX001.